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WVE-210201

Oligonucleotide (Antisense oligonucleotide) · Gene silencing: dystrophin (DMD) · developed by Wave Life Sciences

Phase 2/3 Most advanced trial (none active)

WVE Developer

2 Registered trials

What is WVE-210201?

WVE-210201 is a stereopure antisense oligonucleotide designed to modulate dystrophin expression. It is being studied in Duchenne muscular dystrophy.

Summary written with AI from the sources listed at the end of this page.

At a glance

Drug type: Oligonucleotide (Antisense oligonucleotide)
Targets: dystrophin (DMD)
Mechanism: Gene silencing: dystrophin (DMD)
Therapy area: Neurology
Developer: Wave Life Sciences (WVE)
FDA status: Investigational, not approved in the US. Most advanced trial: Phase 2/3
UNII: IBX8A21EH6

🧪 Clinical trials

Trial	Phase	Condition	Status	Sponsor
NCT03907072	Phase 2/3	Duchenne Muscular Dystrophy	Terminated	WVE
NCT03508947	Phase 1	Duchenne Muscular Dystrophy	Completed	WVE

Trials of the companies BioRadar tracks, from ClinicalTrials.gov, most advanced phase first.

Conditions studied

Duchenne Muscular Dystrophy

Other drugs acting on DMD

WVE-N531 Phase 1/2

More from Wave Life Sciences

WVE-003 Phase 1/2 WVE-004 Phase 1/2 WVE-006 Phase 1/2 WVE-007 Phase 1/2 WVE-120101 Phase 1/2 WVE-120102 Phase 1/2 WVE-N531 Phase 1/2

Sources

ClinicalTrials.gov NCT03508947

Updated Oct 3, 2026. Something wrong or missing? Report it on the WVE page.

Follow WVE, the company behind WVE-210201

See WVE's upcoming FDA decisions, trial readouts, cash runway and dilution risk, updated every day from SEC, FDA and ClinicalTrials.gov filings.

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Data: FDA (Drugs@FDA, Purple Book, DailyMed), NIH (NCI Thesaurus, GSRS, RxNorm), ClinicalTrials.gov • Informational purposes only, not medical or investment advice. • All drugs A–Z